Details for: RPE65

Gene ID: 6121

Symbol: RPE65

Ensembl ID: ENSG00000116745

Description: retinoid isomerohydrolase RPE65

Associated with

Cells (max top 100)

(Cell Significance Index and respective Thresholds are uniquely calculated using our advanced thresholding algorithms to reveal cell-specific gene markers)

  • Cell Name: ciliated cell of the bronchus (CL0002332)
    Fold Change: 2.4090
    Cell Significance Index: -2.3000
  • Cell Name: precursor B cell (CL0000817)
    Fold Change: 1.6546
    Cell Significance Index: 21.4100
  • Cell Name: eye photoreceptor cell (CL0000287)
    Fold Change: 1.3482
    Cell Significance Index: 84.9700
  • Cell Name: megakaryocyte-erythroid progenitor cell (CL0000050)
    Fold Change: 0.9232
    Cell Significance Index: 12.6600
  • Cell Name: retinal rod cell (CL0000604)
    Fold Change: 0.6048
    Cell Significance Index: 7.2100
  • Cell Name: medial ganglionic eminence derived interneuron (CL4023063)
    Fold Change: 0.5876
    Cell Significance Index: 8.4200
  • Cell Name: photoreceptor cell (CL0000210)
    Fold Change: 0.3952
    Cell Significance Index: 5.5500
  • Cell Name: retinal pigment epithelial cell (CL0002586)
    Fold Change: 0.1460
    Cell Significance Index: 1.5700
  • Cell Name: enteric smooth muscle cell (CL0002504)
    Fold Change: 0.0803
    Cell Significance Index: 0.4200
  • Cell Name: lens fiber cell (CL0011004)
    Fold Change: 0.0387
    Cell Significance Index: 1.2300
  • Cell Name: cardiac endothelial cell (CL0010008)
    Fold Change: 0.0146
    Cell Significance Index: 0.2100
  • Cell Name: smooth muscle cell of sphincter of pupil (CL0002243)
    Fold Change: 0.0143
    Cell Significance Index: 1.4900
  • Cell Name: CD14-low, CD16-positive monocyte (CL0002396)
    Fold Change: 0.0074
    Cell Significance Index: 0.1800
  • Cell Name: obsolete caudal ganglionic eminence derived GABAergic cortical interneuron (CL4023070)
    Fold Change: 0.0070
    Cell Significance Index: 2.5200
  • Cell Name: pigmented epithelial cell (CL0000529)
    Fold Change: 0.0044
    Cell Significance Index: 8.2500
  • Cell Name: secondary lens fiber (CL0002225)
    Fold Change: 0.0009
    Cell Significance Index: 1.2200
  • Cell Name: anterior lens cell (CL0002223)
    Fold Change: 0.0000
    Cell Significance Index: 0.0400
  • Cell Name: lens epithelial cell (CL0002224)
    Fold Change: -0.0005
    Cell Significance Index: -0.7500
  • Cell Name: type B pancreatic cell (CL0000169)
    Fold Change: -0.0014
    Cell Significance Index: -0.7900
  • Cell Name: cell in vitro (CL0001034)
    Fold Change: -0.0027
    Cell Significance Index: -1.4900
  • Cell Name: non-pigmented ciliary epithelial cell (CL0002304)
    Fold Change: -0.0030
    Cell Significance Index: -1.8800
  • Cell Name: pancreatic A cell (CL0000171)
    Fold Change: -0.0030
    Cell Significance Index: -2.2100
  • Cell Name: ciliary muscle cell (CL1000443)
    Fold Change: -0.0036
    Cell Significance Index: -1.6300
  • Cell Name: L2/3-6 intratelencephalic projecting glutamatergic neuron (CL4023040)
    Fold Change: -0.0042
    Cell Significance Index: -0.8400
  • Cell Name: retinal blood vessel endothelial cell (CL0002585)
    Fold Change: -0.0062
    Cell Significance Index: -0.0800
  • Cell Name: dopaminergic neuron (CL0000700)
    Fold Change: -0.0066
    Cell Significance Index: -1.9100
  • Cell Name: pigmented ciliary epithelial cell (CL0002303)
    Fold Change: -0.0085
    Cell Significance Index: -1.2300
  • Cell Name: neoplastic cell (CL0001063)
    Fold Change: -0.0099
    Cell Significance Index: -1.9700
  • Cell Name: pancreatic acinar cell (CL0002064)
    Fold Change: -0.0101
    Cell Significance Index: -1.7200
  • Cell Name: stromal cell of ovary (CL0002132)
    Fold Change: -0.0124
    Cell Significance Index: -1.7000
  • Cell Name: mature NK T cell (CL0000814)
    Fold Change: -0.0124
    Cell Significance Index: -0.1400
  • Cell Name: epithelial cell of stomach (CL0002178)
    Fold Change: -0.0152
    Cell Significance Index: -1.7700
  • Cell Name: lactocyte (CL0002325)
    Fold Change: -0.0166
    Cell Significance Index: -2.1400
  • Cell Name: skeletal muscle fiber (CL0008002)
    Fold Change: -0.0166
    Cell Significance Index: -0.4300
  • Cell Name: pancreatic ductal cell (CL0002079)
    Fold Change: -0.0170
    Cell Significance Index: -1.9500
  • Cell Name: obsolete epithelial cell of alveolus of lung (CL0010003)
    Fold Change: -0.0192
    Cell Significance Index: -0.4800
  • Cell Name: abnormal cell (CL0001061)
    Fold Change: -0.0209
    Cell Significance Index: -2.1300
  • Cell Name: glycinergic neuron (CL1001509)
    Fold Change: -0.0213
    Cell Significance Index: -1.1200
  • Cell Name: forebrain neuroblast (CL1000042)
    Fold Change: -0.0225
    Cell Significance Index: -1.3800
  • Cell Name: basal epithelial cell of tracheobronchial tree (CL0002329)
    Fold Change: -0.0253
    Cell Significance Index: -0.7100
  • Cell Name: myometrial cell (CL0002366)
    Fold Change: -0.0278
    Cell Significance Index: -0.3200
  • Cell Name: acinar cell of salivary gland (CL0002623)
    Fold Change: -0.0287
    Cell Significance Index: -1.3400
  • Cell Name: megakaryocyte (CL0000556)
    Fold Change: -0.0290
    Cell Significance Index: -0.4700
  • Cell Name: progenitor cell of mammary luminal epithelium (CL0009116)
    Fold Change: -0.0316
    Cell Significance Index: -2.3600
  • Cell Name: cardiac muscle myoblast (CL0000513)
    Fold Change: -0.0336
    Cell Significance Index: -2.5800
  • Cell Name: keratocyte (CL0002363)
    Fold Change: -0.0340
    Cell Significance Index: -0.5400
  • Cell Name: hippocampal granule cell (CL0001033)
    Fold Change: -0.0344
    Cell Significance Index: -2.3100
  • Cell Name: plasmacytoid dendritic cell (CL0000784)
    Fold Change: -0.0347
    Cell Significance Index: -0.4600
  • Cell Name: retinal cone cell (CL0000573)
    Fold Change: -0.0360
    Cell Significance Index: -0.4500
  • Cell Name: corticothalamic-projecting glutamatergic cortical neuron (CL4023013)
    Fold Change: -0.0396
    Cell Significance Index: -1.2600
  • Cell Name: fibro/adipogenic progenitor cell (CL0009099)
    Fold Change: -0.0396
    Cell Significance Index: -2.0000
  • Cell Name: retinal progenitor cell (CL0002672)
    Fold Change: -0.0412
    Cell Significance Index: -2.3100
  • Cell Name: lung endothelial cell (CL1001567)
    Fold Change: -0.0436
    Cell Significance Index: -2.2700
  • Cell Name: basal cell of prostate epithelium (CL0002341)
    Fold Change: -0.0456
    Cell Significance Index: -1.2400
  • Cell Name: indirect pathway medium spiny neuron (CL4023029)
    Fold Change: -0.0461
    Cell Significance Index: -2.0400
  • Cell Name: L5 extratelencephalic projecting glutamatergic cortical neuron (CL4023041)
    Fold Change: -0.0465
    Cell Significance Index: -1.6300
  • Cell Name: retinal bipolar neuron (CL0000748)
    Fold Change: -0.0470
    Cell Significance Index: -0.5700
  • Cell Name: periportal region hepatocyte (CL0019026)
    Fold Change: -0.0474
    Cell Significance Index: -0.7000
  • Cell Name: L6b glutamatergic cortical neuron (CL4023038)
    Fold Change: -0.0476
    Cell Significance Index: -1.5600
  • Cell Name: hippocampal astrocyte (CL0002604)
    Fold Change: -0.0479
    Cell Significance Index: -0.6700
  • Cell Name: luminal adaptive secretory precursor cell of mammary gland (CL4033057)
    Fold Change: -0.0484
    Cell Significance Index: -2.2800
  • Cell Name: erythrocyte (CL0000232)
    Fold Change: -0.0510
    Cell Significance Index: -1.3000
  • Cell Name: mesangial cell (CL0000650)
    Fold Change: -0.0522
    Cell Significance Index: -0.6600
  • Cell Name: keratinocyte (CL0000312)
    Fold Change: -0.0525
    Cell Significance Index: -1.3100
  • Cell Name: melanocyte (CL0000148)
    Fold Change: -0.0544
    Cell Significance Index: -0.5100
  • Cell Name: astrocyte of the cerebral cortex (CL0002605)
    Fold Change: -0.0544
    Cell Significance Index: -0.9400
  • Cell Name: early T lineage precursor (CL0002425)
    Fold Change: -0.0551
    Cell Significance Index: -0.8000
  • Cell Name: direct pathway medium spiny neuron (CL4023026)
    Fold Change: -0.0552
    Cell Significance Index: -2.0900
  • Cell Name: cortical cell of adrenal gland (CL0002097)
    Fold Change: -0.0567
    Cell Significance Index: -1.5200
  • Cell Name: mesothelial cell of epicardium (CL0011019)
    Fold Change: -0.0570
    Cell Significance Index: -0.4900
  • Cell Name: neuron associated cell (CL0000095)
    Fold Change: -0.0593
    Cell Significance Index: -2.4300
  • Cell Name: mesenchymal cell (CL0008019)
    Fold Change: -0.0603
    Cell Significance Index: -1.0100
  • Cell Name: glioblast (CL0000030)
    Fold Change: -0.0605
    Cell Significance Index: -0.3800
  • Cell Name: type I muscle cell (CL0002211)
    Fold Change: -0.0619
    Cell Significance Index: -1.5100
  • Cell Name: hematopoietic stem cell (CL0000037)
    Fold Change: -0.0638
    Cell Significance Index: -1.0900
  • Cell Name: thymocyte (CL0000893)
    Fold Change: -0.0641
    Cell Significance Index: -0.8100
  • Cell Name: cytotoxic T cell (CL0000910)
    Fold Change: -0.0642
    Cell Significance Index: -0.9400
  • Cell Name: peg cell (CL4033014)
    Fold Change: -0.0658
    Cell Significance Index: -1.5200
  • Cell Name: fibroblast of dermis (CL0002551)
    Fold Change: -0.0659
    Cell Significance Index: -1.3800
  • Cell Name: cerebellar granule cell (CL0001031)
    Fold Change: -0.0662
    Cell Significance Index: -1.1300
  • Cell Name: sst GABAergic cortical interneuron (CL4023017)
    Fold Change: -0.0733
    Cell Significance Index: -1.4500
  • Cell Name: cortical interneuron (CL0008031)
    Fold Change: -0.0742
    Cell Significance Index: -1.7800
  • Cell Name: CD4-positive, alpha-beta thymocyte (CL0000810)
    Fold Change: -0.0754
    Cell Significance Index: -1.3000
  • Cell Name: PP cell (CL0000696)
    Fold Change: -0.0757
    Cell Significance Index: -0.7700
  • Cell Name: astrocyte (CL0000127)
    Fold Change: -0.0769
    Cell Significance Index: -0.8800
  • Cell Name: preadipocyte (CL0002334)
    Fold Change: -0.0794
    Cell Significance Index: -1.5500
  • Cell Name: near-projecting glutamatergic cortical neuron (CL4023012)
    Fold Change: -0.0802
    Cell Significance Index: -2.0000
  • Cell Name: hippocampal pyramidal neuron (CL1001571)
    Fold Change: -0.0802
    Cell Significance Index: -2.2900
  • Cell Name: fibroblast of mammary gland (CL0002555)
    Fold Change: -0.0816
    Cell Significance Index: -2.3400
  • Cell Name: granulosa cell (CL0000501)
    Fold Change: -0.0859
    Cell Significance Index: -2.2600
  • Cell Name: placental villous trophoblast (CL2000060)
    Fold Change: -0.0861
    Cell Significance Index: -2.3000
  • Cell Name: caudal ganglionic eminence derived cortical interneuron (CL4023064)
    Fold Change: -0.0863
    Cell Significance Index: -1.7200
  • Cell Name: luminal cell of prostate epithelium (CL0002340)
    Fold Change: -0.0899
    Cell Significance Index: -0.9300
  • Cell Name: pvalb GABAergic cortical interneuron (CL4023018)
    Fold Change: -0.0900
    Cell Significance Index: -1.9100
  • Cell Name: squamous epithelial cell (CL0000076)
    Fold Change: -0.0904
    Cell Significance Index: -1.1000
  • Cell Name: lamp5 GABAergic cortical interneuron (CL4023011)
    Fold Change: -0.0940
    Cell Significance Index: -2.0300
  • Cell Name: type II muscle cell (CL0002212)
    Fold Change: -0.0948
    Cell Significance Index: -1.5300
  • Cell Name: skeletal muscle fibroblast (CL0011027)
    Fold Change: -0.0969
    Cell Significance Index: -0.6600
  • Cell Name: decidual cell (CL2000002)
    Fold Change: -0.0975
    Cell Significance Index: -1.5700
  • Cell Name: corneal endothelial cell (CL0000132)
    Fold Change: -0.0986
    Cell Significance Index: -1.5000

Cell ID: Standard Cell Ontology term used for mapping and comparing cells across experiments. Ensures consistency in analyzing cellular functions across tissues.
Fold Change: Represents the ratio of the current Cell Significance Index to the Cell Significance Index Threshold, indicating how much the gene expression has changed compared to a baseline.
Cell Significance Index: Reflects how strongly a gene is expressed in this specific cell.

Cell ID: Standard Cell Ontology term used for mapping and comparing cells across experiments. Ensures consistency in analyzing cellular functions across tissues.
Fold Change: Represents the ratio of the current Cell Significance Index to the Cell Significance Index Threshold, indicating how much the gene expression has changed compared to a baseline.
Cell Significance Index: Reflects how strongly a gene is expressed in this cell type. Calculated using techniques like effect size estimation and bootstrapping for reliability.

Cell ID: Standard Cell Ontology term used for mapping and comparing cells across experiments. Ensures consistency in analyzing cellular functions across tissues.
Fold Change: Represents the ratio of the current Cell Significance Index to the Cell Significance Index Threshold, indicating how much the gene expression has changed compared to a baseline.
Cell Significance Index: Reflects how strongly a gene is expressed in this cell type. Calculated using techniques like effect size estimation and bootstrapping for reliability.

Other Information

**Key Characteristics:** 1. **Retinoid Metabolizing Enzyme:** RPE65 is a retinoid isomerase that hydrolyzes all-trans-retinyl esters, a crucial step in the regeneration of retinal metabolites. 2. **Visual Perception:** The RPE65 protein is essential for the detection of light stimuli and visual perception, particularly in the canonical retinoid cycle in rods (twilight vision). 3. **Cellular Expression:** RPE65 is significantly expressed in various cell types, including those in the retina, nervous system, and immune cells. 4. **Enzyme Activity:** RPE65 exhibits a range of enzymatic activities, including all-trans-retinyl-palmitate hydrolase, 11-cis retinol forming activity, and isomerase activity. **Pathways and Functions:** 1. **Retinoid Metabolic Process:** RPE65 is involved in the hydrolysis of all-trans-retinyl esters, which regenerates retinal metabolites essential for visual perception. 2. **Visual Phototransduction:** The RPE65 protein is critical for the detection of light stimuli and visual perception, particularly in the canonical retinoid cycle in rods (twilight vision). 3. **Cardiolipin Binding:** RPE65 exhibits cardiolipin binding activity, which may play a role in its enzymatic function. 4. **Cellular Homeostasis:** The RPE65 protein is involved in maintaining retinal homeostasis, which is essential for visual perception and overall health. **Clinical Significance:** 1. **Retinal Disorders:** Abnormalities in the RPE65 gene have been linked to retinal disorders, such as retinitis pigmentosa, a group of genetic disorders that affect the retina and lead to progressive vision loss. 2. **Visual Impairment:** RPE65 dysfunction has been implicated in visual impairment, including night blindness and impaired visual acuity. 3. **Neurodegenerative Diseases:** The RPE65 protein may also play a role in neurodegenerative diseases, such as Alzheimer's disease and Parkinson's disease, which affect the nervous system and retina. 4. **Cancer:** Aberrant RPE65 expression has been observed in certain types of cancer, suggesting its potential role in tumorigenesis. In conclusion, the RPE65 gene plays a critical role in the visual system and retinoid metabolism, and its dysfunction has been implicated in various retinal disorders and visual impairments. Further research is necessary to fully understand the functional significance of RPE65 and its potential therapeutic applications.

Genular Protein ID: 4101424718

Symbol: RPE65_HUMAN

Name: All-trans-retinyl-palmitate hydrolase

UniProtKB Accession Codes:

Database IDs:

Citations:

PubMed ID: 7633413

Title: Molecular characterization of the human gene encoding an abundant 61 kDa protein specific to the retinal pigment epithelium.

PubMed ID: 7633413

DOI: 10.1093/hmg/4.4.641

PubMed ID: 9501220

Title: Mutations in the RPE65 gene in patients with autosomal recessive retinitis pigmentosa or Leber congenital amaurosis.

PubMed ID: 9501220

DOI: 10.1073/pnas.95.6.3088

PubMed ID: 14702039

Title: Complete sequencing and characterization of 21,243 full-length human cDNAs.

PubMed ID: 14702039

DOI: 10.1038/ng1285

PubMed ID: 16710414

Title: The DNA sequence and biological annotation of human chromosome 1.

PubMed ID: 16710414

DOI: 10.1038/nature04727

PubMed ID: 15489334

Title: The status, quality, and expansion of the NIH full-length cDNA project: the Mammalian Gene Collection (MGC).

PubMed ID: 15489334

DOI: 10.1101/gr.2596504

PubMed ID: 19049981

Title: Identification of a novel palmitylation site essential for membrane association and isomerohydrolase activity of RPE65.

PubMed ID: 19049981

DOI: 10.1074/jbc.m807248200

PubMed ID: 16198348

Title: Identification of conserved histidines and glutamic acid as key residues for isomerohydrolase activity of RPE65, an enzyme of the visual cycle in the retinal pigment epithelium.

PubMed ID: 16198348

DOI: 10.1016/j.febslet.2005.09.002

PubMed ID: 16116091

Title: RPE65 is the isomerohydrolase in the retinoid visual cycle.

PubMed ID: 16116091

DOI: 10.1073/pnas.0503460102

PubMed ID: 17848510

Title: Human cone photoreceptor dependence on RPE65 isomerase.

PubMed ID: 17848510

DOI: 10.1073/pnas.0706367104

PubMed ID: 21493626

Title: The Usher 1B protein, MYO7A, is required for normal localization and function of the visual retinoid cycle enzyme, RPE65.

PubMed ID: 21493626

DOI: 10.1093/hmg/ddr155

PubMed ID: 25112876

Title: Identification of key residues determining isomerohydrolase activity of human RPE65.

PubMed ID: 25112876

DOI: 10.1074/jbc.m114.558619

PubMed ID: 28874556

Title: RPE65 has an additional function as the lutein to meso-zeaxanthin isomerase in the vertebrate eye.

PubMed ID: 28874556

DOI: 10.1073/pnas.1706332114

PubMed ID: 9326927

Title: Mutations in RPE65 cause Leber's congenital amaurosis.

PubMed ID: 9326927

DOI: 10.1038/ng1097-139

PubMed ID: 9326941

Title: Mutations in RPE65 cause autosomal recessive childhood-onset severe retinal dystrophy.

PubMed ID: 9326941

DOI: 10.1038/ng1097-194

PubMed ID: 9801879

Title: Autosomal recessive retinal dystrophy associated with two novel mutations in the RPE65 gene.

PubMed ID: 9801879

DOI: 10.1038/sj.ejhg.5200205

PubMed ID: 10090910

Title: Different functional outcome of RetGC1 and RPE65 gene mutations in Leber congenital amaurosis.

PubMed ID: 10090910

DOI: 10.1086/302335

PubMed ID: 10766140

Title: Mutation analysis of 3 genes in patients with Leber congenital amaurosis.

PubMed ID: 10766140

DOI: 10.1001/archopht.118.4.538

PubMed ID: 11095629

Title: Genetics and phenotypes of RPE65 mutations in inherited retinal degeneration.

PubMed ID: 11095629

PubMed ID: 11462243

Title: Four novel mutations in the RPE65 gene in patients with Leber congenital amaurosis.

PubMed ID: 11462243

DOI: 10.1002/humu.1168

PubMed ID: 12960219

Title: A Tyr368His RPE65 founder mutation is associated with variable expression and progression of early onset retinal dystrophy in 10 families of a genetically isolated population.

PubMed ID: 12960219

DOI: 10.1136/jmg.40.9.709

PubMed ID: 14611946

Title: Analysis of three genes in Leber congenital amaurosis in Indonesian patients.

PubMed ID: 14611946

DOI: 10.1016/j.visres.2003.08.008

PubMed ID: 14962443

Title: Thirty-year follow-up of a patient with Leber congenital amaurosis and novel RPE65 mutations.

PubMed ID: 14962443

DOI: 10.1016/s0002-9394(03)00913-9

PubMed ID: 15024725

Title: Leber congenital amaurosis: comprehensive survey of the genetic heterogeneity, refinement of the clinical definition, and genotype-phenotype correlations as a strategy for molecular diagnosis.

PubMed ID: 15024725

DOI: 10.1002/humu.20010

PubMed ID: 15557452

Title: A homozygosity-based search for mutations in patients with autosomal recessive retinitis pigmentosa, using microsatellite markers.

PubMed ID: 15557452

DOI: 10.1167/iovs.04-0544

PubMed ID: 16205573

Title: Evaluation of genotype-phenotype associations in Leber congenital amaurosis.

PubMed ID: 16205573

DOI: 10.1097/00006982-200510000-00016

PubMed ID: 17297704

Title: Gene symbol: RPE65. Disease: Leber's congenital amaurosis. Accession #Hm0548.

PubMed ID: 17297704

PubMed ID: 17964524

Title: Leber congenital amaurosis - a model for efficient genetic testing of heterogeneous disorders: LXIV Edward Jackson Memorial Lecture.

PubMed ID: 17964524

DOI: 10.1016/j.ajo.2007.08.022

PubMed ID: 17724218

Title: Clinical and molecular genetics of Leber's congenital amaurosis: a multicenter study of Italian patients.

PubMed ID: 17724218

DOI: 10.1167/iovs.07-0068

PubMed ID: 18682808

Title: Molecular characterization of Leber congenital amaurosis in Koreans.

PubMed ID: 18682808

PubMed ID: 19431183

Title: Predicting the pathogenicity of RPE65 mutations.

PubMed ID: 19431183

DOI: 10.1002/humu.21033

PubMed ID: 21654732

Title: A dominant mutation in RPE65 identified by whole-exome sequencing causes retinitis pigmentosa with choroidal involvement.

PubMed ID: 21654732

DOI: 10.1038/ejhg.2011.86

PubMed ID: 27307694

Title: The clinical features of retinal disease due to a dominant mutation in RPE65.

PubMed ID: 27307694

PubMed ID: 29659842

Title: Insights into the pathogenesis of dominant retinitis pigmentosa associated with a D477G mutation in RPE65.

PubMed ID: 29659842

DOI: 10.1093/hmg/ddy128

PubMed ID: 21602930

Title: Detection of variants in 15 genes in 87 unrelated Chinese patients with Leber congenital amaurosis.

PubMed ID: 21602930

DOI: 10.1371/journal.pone.0019458

PubMed ID: 22334370

Title: Next-generation genetic testing for retinitis pigmentosa.

PubMed ID: 22334370

DOI: 10.1002/humu.22045

PubMed ID: 22509104

Title: Novel RPE65 mutations associated with Leber congenital amaurosis in Chinese patients.

PubMed ID: 22509104

PubMed ID: 23878505

Title: Novel mutations in RPE65 identified in consanguineous Pakistani families with retinal dystrophy.

PubMed ID: 23878505

PubMed ID: 27535533

Title: Analysis of protein-coding genetic variation in 60,706 humans.

PubMed ID: 27535533

DOI: 10.1038/nature19057

PubMed ID: 28418496

Title: Homozygosity Mapping and Genetic Analysis of Autosomal Recessive Retinal Dystrophies in 144 Consanguineous Pakistani Families.

PubMed ID: 28418496

DOI: 10.1167/iovs.17-21424

PubMed ID: 30628748

Title: Aberrant RNA splicing is the major pathogenic effect in a knock-in mouse model of the dominantly inherited c.1430A>G human RPE65 mutation.

PubMed ID: 30628748

DOI: 10.1002/humu.23706

Sequence Information:

  • Length: 533
  • Mass: 60948
  • Checksum: 7193C93F3325798D
  • Sequence:
  • MSIQVEHPAG GYKKLFETVE ELSSPLTAHV TGRIPLWLTG SLLRCGPGLF EVGSEPFYHL 
    FDGQALLHKF DFKEGHVTYH RRFIRTDAYV RAMTEKRIVI TEFGTCAFPD PCKNIFSRFF 
    SYFRGVEVTD NALVNVYPVG EDYYACTETN FITKINPETL ETIKQVDLCN YVSVNGATAH 
    PHIENDGTVY NIGNCFGKNF SIAYNIVKIP PLQADKEDPI SKSEIVVQFP CSDRFKPSYV 
    HSFGLTPNYI VFVETPVKIN LFKFLSSWSL WGANYMDCFE SNETMGVWLH IADKKRKKYL 
    NNKYRTSPFN LFHHINTYED NGFLIVDLCC WKGFEFVYNY LYLANLRENW EEVKKNARKA 
    PQPEVRRYVL PLNIDKADTG KNLVTLPNTT ATAILCSDET IWLEPEVLFS GPRQAFEFPQ 
    INYQKYCGKP YTYAYGLGLN HFVPDRLCKL NVKTKETWVW QEPDSYPSEP IFVSHPDALE 
    EDDGVVLSVV VSPGAGQKPA YLLILNAKDL SEVARAEVEI NIPVTFHGLF KKS

Database document:

This is a preview of the gene's schema. Only a few entries are kept for 'singleCellExpressions,' 'mRNAExpressions,' and other large data arrays for visualization purposes. You can zoom in with the mouse wheel for a closer view, and the text will adjust automatically if necessary. For the full schema, download it here.